Use precise geolocation data and actively scan device characteristics for identification. This is done to store and access ...
Treatment with Spinraza (nusinersen) can help stabilize or improve motor function in adults with SMA, according to a new ...
Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...
A rare genetic condition, Spinal Muscular Atrophy (SMA) affects one in 7,000 people in India. It mostly affects children and ...
Chugai Pharma’s Evrysdi tablets 5mg receives Japanese approval to treat spinal muscular atrophy: Saturday, March 29, 2025, 11:00 Hrs [IST] Chugai Pharmaceutical Co., Ltd. announ ...
A Prescription Drug User Fee Act (PDUFA) target action date for apitegromab has been set for Sept. 22, 2025.
Apitegromab, a fully human monoclonal antibody, works by selectively binding to the pro- and latent forms of myostatin in order to inhibit myostatin activation.
Video: Spinal Muscular Atrophy: When is Surgical Intervention Appropriate? —How does one time surgery for scoliosis in children with pediatric spinal muscular atrophy get a maximum benefit ...
The high court noted that SMA is a debilitating disease which has no cure, and the only approved drug, Risdiplam, marketed ...
Apitegromab is an investigational treatment aimed at improving motor function for people living with spinal muscular atrophy. Scholar Rock said it has also submitted and received validation for its ...
The bench said that public good outweighs the company’s profit as the drug is not available at an affordable price in India.